Mark DeWitt and Don Kohn Discuss Their ex vivo CRISPR-based Therapy to Cure Sickle Cell Anemia
CRISPR Cuts20 Loka 2023

Mark DeWitt and Don Kohn Discuss Their ex vivo CRISPR-based Therapy to Cure Sickle Cell Anemia

Dr. Mark DeWitt Ph.D., Associate Director at Mammoth Biosciences, and Dr. Don Kohn M.D., distinguished professor and Director of the UCLA Human Gene and Cell Therapy Program and CIRM grantee sat down with us to discuss their latest clinical trials to cure sickle cell anemia, how synthetic guides accelerated their journey from the bench to the clinic, and their experience in the cell and gene therapy space.

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Imran House and Junyun Lai Discuss CRISPR Screening in Immuno-Oncology

Imran House and Junyun Lai Discuss CRISPR Screening in Immuno-Oncology

Imran House, Ph.D. and Junyun Lai Ph.D. are Senior Scientists at the biotech start-up, oNKo-Innate in Melbourne, Australia that focuses on developing immuno-oncology therapies. In this episode, they d...

31 Tammi 202426min

Dina Simkin Breaks Down Epilepsy Cell Modeling

Dina Simkin Breaks Down Epilepsy Cell Modeling

Dina Simkin, Professor of Neurology at Northwestern University, joins us in this episode of CRISPR Cuts. Dr. Simkin talks about her path to becoming a researcher, art, and the importance of patient an...

16 Touko 202327min

Sunil Sharma and Raffaella Soldi Talk CRISPR For Unbiased Drug Screening for Rare Pediatric Cancers

Sunil Sharma and Raffaella Soldi Talk CRISPR For Unbiased Drug Screening for Rare Pediatric Cancers

Dr. Sunil Sharma and Dr. Raffaella Soldi of the Translational Genomics Research Institute chat about using CRISPR arrayed screens to identify novel drug targets for Ewing's Sarcoma, outlooks for the f...

24 Huhti 202324min

Stephanie Cherqui Discusses Clinical Development of CRISPR Therapies for Rare Diseases

Stephanie Cherqui Discusses Clinical Development of CRISPR Therapies for Rare Diseases

Professor Stephanie Cherqui, UCSD, has worked on the development of cell therapies for two rare genetic diseases, cystinosis and Friedreich’s ataxia. In this interview, Dr. Cherqui chats about her exp...

20 Maalis 202320min

Christian Groendahl On Pioneering a CRISPR-based Microbial Gene Therapy

Christian Groendahl On Pioneering a CRISPR-based Microbial Gene Therapy

Tune in to hear Christian Groendahl, CEO of SNIPR Biome, talk about CRISPR editing in prokaryotes, their novel E. coli-targeting CRISPR therapy trials, and his experiences and vision leading a start u...

5 Joulu 202229min

Bryan Dechairo Envisions an Accessible Future for CRISPR Diagnostics

Bryan Dechairo Envisions an Accessible Future for CRISPR Diagnostics

In this episode, Bryan Dechairo, CEO of Sherlock Biosciences, talks about the impact of technology advances in the field of CRISPR diagnostics, his experiences leading Sherlock Biosciences, and his te...

6 Syys 202235min

Ayal Hendel Talks About CRISPR in Bubble Boy Disease

Ayal Hendel Talks About CRISPR in Bubble Boy Disease

Dr. Ayal Hendel, a genome-editing pioneer and group leader at Bar Ilan University in Israel, was one of the first researchers to use modified synthetic sgRNA to edit primary cells with CRISPR. In this...

7 Kesä 202235min

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