Genes and Your Health Series: mRNA: What it is, What it Does, and Hope in Rare Diseases
Mayo Clinic Talks24 Huhti 2025

Genes and Your Health Series: mRNA: What it is, What it Does, and Hope in Rare Diseases

Host: Denise M. Dupras, M.D., Ph.D.

Guest: Michael Zimmer, Ph.D., Director of Rare Diseases at Moderna Therapeutics

This episode of Genes & Your Health welcomes Dr. Michael Zimmer from Moderna Therapeutics, who discusses how mRNA technology is being applied to treat rare genetic diseases, especially liver-based metabolic disorders. Dr. Zimmer explains how mRNA can help the body produce missing proteins, the challenges of delivering these therapies, and the promise they hold for previously untreatable conditions.

Connect with us and learn more here: https://ce.mayo.edu/online-education/content/mayo-clinic-podcasts

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