Living With Cystic Fibrosis13 Maj 2024

The Final 10 percent

Approximately 10 percent of the CF population is waiting for a CF modulator drug that will help them by correcting the underlying condition of their disease. Current modulator drugs help more common CF mutations. Emily Kramer Golinkoff is one of the people who doesn't have a CF modulator that will help her. Her Foundation, Emily's Entourage, is a leader in research. They are focusing on people with CF who have the nonsense mutation.

On Emily's team is Dr. Chandra Ghose, who is the Chief Scientific Officer. Dr. Ghose founded Bioharmony Therapeutics, an early stage biotech startup that specialized in the development of novel antimicrobials, to combat drug resistant bacterial infections.

Chandra spent 8 years at the Aaron Diamond AIDS Research Center where she focused her research on developing life saving vaccines in the laboratory of Dr. David Ho. Chandra earned her PhD from New York University School of Medicine in microbiology and her bachelors degree from Saint Louis University in biology and theology, splitting her time between the U.S. and Spain campuses.

For more information about Emily's Entourage: https://www.emilysentourage.org

For registry information: https://www.emilysentourage.org/cystic-fibrosis-patient-registry/

For Emily's Entourage information: https://www.emilysentourage.org/eeupdates/

Follow EE at: @emilysentourage

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