Spinraza for Most SMA Patients in China & Ben Mattlin's Book on Inter-abled Relationships

Spinraza for Most SMA Patients in China & Ben Mattlin's Book on Inter-abled Relationships

We discuss how China has approved Spinraza for most SMA patients. Also, Community Editor Kevin Schaefer reads from his review of a book about inter-abled relationships by Ben Mattlin. Mattlin is a Los Angeles-based writer with SMA Type 2, and this review is available on our main website and on our forums. Are you interested in understanding gene therapy? ExploreGeneTherapy.com has helpful information about gene therapy, including its history and how it is being investigated for the treatment of genetic diseases. Visit www.exploregenetherapy.com

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Neurofilaments May Not Be Biomarker for Older Patients & The New CDC Mask Recommendations

Neurofilaments May Not Be Biomarker for Older Patients & The New CDC Mask Recommendations

SMA News Today’s multimedia associate, Price Wooldridge, discusses how neurofilaments may not be a biomarker for older patients with Spinal Muscular Atrophy (SMA) Type 1. Also, DeAnn Runge discusses ...

21 Maj 20218min

Warning of TMA, Rare Blood Disorder, Added to Zolgensma’s Safety Label & Friendships and SMA

Warning of TMA, Rare Blood Disorder, Added to Zolgensma’s Safety Label & Friendships and SMA

SMA News Today’s multimedia associate, Price Wooldridge, discusses adding thrombotic microangiopathy (TMA) to the list of safety concerns for Zolgensma. Also, Forums Director Kevin Schaefer reads a c...

19 Maj 20219min

#82: Interview with Hawken Miller, Journalist with Muscular Dystrophy

#82: Interview with Hawken Miller, Journalist with Muscular Dystrophy

In episode 82, host Kevin Schaefer talks with Hawken Miller from Newport Beach, California. Hawken is a features writer for SMA News Today’s parent company, BioNews, as well as a columnist for Muscula...

18 Maj 202136min

Sex And The Number of Copies of The SMN 2 Gene Can Influence Age of Onset for SMA Type 3 Patients

Sex And The Number of Copies of The SMN 2 Gene Can Influence Age of Onset for SMA Type 3 Patients

SMA News Today’s multimedia associate, Price Wooldridge, discusses how sex, and the number of copies of the SMN 2 gene influence age of onset for Spinal Muscular Atrophy Type 3 patients. Also, DeAnn ...

17 Maj 202113min

UK NICE Expands Access to Spinraza for SMA Type 3 & The Disappointment of a Jaco Robotic Arm Denial

UK NICE Expands Access to Spinraza for SMA Type 3 & The Disappointment of a Jaco Robotic Arm Denial

SMA News Today’s multimedia associate, Price Wooldridge, discusses how UK NICE expands access to Spinraza for Spinal Muscular Atrophy (SMA) Type 3 patients. Also, DeAnn Runge talks about how disappoi...

14 Maj 20216min

German Study Urges Newborn SMA Screening, Citing Better Outcomes & Managing Chaos

German Study Urges Newborn SMA Screening, Citing Better Outcomes & Managing Chaos

SMA News Today’s multimedia associate, Price Wooldridge, discusses a German study which recommends newborn screening for Spinal Muscular Atrophy (SMA), citing better outcomes. Also, Forums Director K...

12 Maj 20219min

Grant Awarded to Find Affordable Treatments for Children & SMA Would You Rather

Grant Awarded to Find Affordable Treatments for Children & SMA Would You Rather

SMA News Today’s multimedia associate, Price Wooldridge, discusses a grant awared to find affordable treatments for children with Spinal Muscular Atrophy (SMA). Also, on the forums a fun game of SMA ...

10 Maj 20215min

Novartis Poised for Phase 3b SMART Study of Zolgensma & SMA Adventures

Novartis Poised for Phase 3b SMART Study of Zolgensma & SMA Adventures

SMA News Today’s multimedia associate, Price Wooldridge, discusses how Novartis is poised for their Phase 3b SMART study of Zolgensma. Also, DeAnn Runge shares a recent adventure she went on to a gre...

7 Maj 20219min

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