How AveXis’ OneGene Program Could Help Families Wanting Zolgensma & Trending Topics
We discuss how AveXis’ OneGene program could smooth the path for families wanting Zolgensma and Community Development Manager Kevin Schaefer talks about some trending discussions in the SMA News Today...
6 Sep 20199min
Future Work Into Zolgensma, Gene Therapy And Other SMA Treatments & Physical Books
SMA News Today’s Director of Multichannel Content, Michael Morale, discusses likely future work into Zolgensma, gene therapies and other SMA treatments. Community Development Manager Kevin Schaefer ta...
4 Sep 201912min
#41 - Roundtable Discussion - Discussion for September 2019
Hosts Kevin Schaefer and Michael Morale discuss a recent webinar about AveXis’ gene therapy Zolgensma. Then in part two, they talk about SMA awareness month, and a couple of our recent columns.
3 Sep 201931min
NORD Honors Industry In Patient Advocates At Rare Impact Awards Gala & Overprotective Parents
We discuss how NORD honors industry in patient advocates at rare impact awards gala and SMA News Today forums moderator DeAnn Runge shares her perspective on overprotective parents. A college friend i...
2 Sep 20198min
Anti-Epileptic Keppra Can Be A Candidate For SMA Treatment & Batcave For Personal Space
We discuss a study that suggests that suggests Anti-epileptic Keppra could be a candidate for treatment of SMA and Community Development Manager Kevin Schaefer reads his latest column about acquiring ...
30 Aug 20198min
Zolgensma’s Arrival Adds Urgency to SMA Newborn Screening Efforts & Natalie Russo And Her Brother
SMA News Today’s Director of Multichannel Content, Michael Morale, discusses how Zolgensma’s arrival adds urgency to SMA newborn screening efforts in the US and Community Development Manager Kevin Sch...
28 Aug 20199min
Eurordis' Integrated Care Initiative For Rare Disease Patients & Cooperate With Physical Therapists
We discuss how Eurordis unveils an integrated care initiative for rare disease patients. Also, SMA News Today’s Director of Multichannel Content, Michael Morale, discusses working with physical therap...
26 Aug 20199min
RNA Molecule miR-23a May Have Therapeutic Role in SMA & From College Writing Course To A Career
We discuss a study that suggests that the small RNA molecule miR-23a, may have a therapeutic role in SMA. Also, Community Development Manager Kevin Schaefer reads from his latest column. In this post,...
23 Aug 20198min
