A ‘Miracle’: Spinraza Gives Boy a Chance to Grow Up & Life Is an Adventure, So Let’s Be Pioneers
SMA News Today’s multimedia associate, Price Wooldridge, discusses a “miracle” when Spinraza gives a boy, now 5 years old, a chance to grow up fast and show good progress. Also, forums Director Kevin...
17 Feb 202114min
#76: Discussing Treatment Updates, Vaccine Access, and Recent Columns
In episode 76, host Kevin Schaefer talks with fellow SMA News Today contributor DeAnn Runge. They discuss news regarding increasing the dosage of Spinraza in SMA patients, updates on Scholar Rock’s tr...
16 Feb 202150min
EMBRACE Trial Supports Spinraza’s Benefits in Broad Range of SMA Patients
SMA News Today’s multimedia associate, Price Wooldridge, discusses the EMBRACE Trial which supports Spinraza’s benefits in a broad range of Spinal Muscular Atrophy (SMA) patients. Also, DeAnn Runge w...
15 Feb 202112min
NORD’s 6th ‘State Report Card’ Notes Progress, Raises Concerns
SMA News Today’s multimedia associate, Price Wooldridge, discusses the National Organization for Rare Disorders (NORD) 6th “state report card”, noting progress, but raising concerns. Plus, closing in...
12 Feb 20217min
Rare Disease Groups, Pharmas Join SMA Europe Push for Newborn Screening
SMA News Today’s multimedia associate, Price Wooldridge, discusses rare disease groups and pharmaceutical companies, joining SMA Europe in a push for newborn screening for Spinal Muscular Atrophy (SMA...
10 Feb 20217min
Motor Function, Breathing Important in Choosing Treatment
SMA News Today’s multimedia associate, Price Wooldridge, discusses improvement in motor function, breathing, and ease of administration are important factors when Spinal Muscular Atrophy (SMA) patient...
8 Feb 20218min
More Severe COVID-19 Symptoms Seen in Children with SMA Type 1
SMA News Today’s multimedia associate, Price Wooldridge, discusses more severe COVID-19 symptoms being seen in children with Spinal Muscular Atrophy (SMA) Type 1. Also, vlogger and forums moderator D...
5 Feb 20217min
Better Ways of Capturing Progression in Types 2 and 3 Identified in Study
SMA News Today’s multimedia associate, Price Wooldridge, discusses better ways of capturing progression of motor abilities in Spinal Muscular Atrophy (SMA) Types 2 and 3. Forums Director Kevin Schaef...
3 Feb 202110min
