193: An Interview With Dr. John Mascarenhas, Professor at New York's Icahn School of Medicine
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews John Mascarenhas, MD, a professor with the Icahn School of Medicine at Mount Sinai in New York, on advancing care in myelofibros...
10 Okt 202517min
192: An Interview With Catherine Miller, PharmD, of Intellia Therapeutics on an Experimental Gene Editing Therapy for HAE
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Catherine Miller, PharmD, global medical affairs lead for hereditary angioedema (HAE) at Intellia Therapeutics, on an experiment...
1 Okt 202513min
191: An Interview With Dr. Shoshana Revel-Vilk, Director of the Gaucher Unit at Israel's Shaare Zedek Medical Center
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Shoshana Revel-Vilk, MD, director of the Gaucher unit at Shaare Zedek Medical Center in Jerusalem, Israel.
24 Sep 202516min
190: An Interview With Nikki McIntosh, Founder of Rare Mamas and SMA Patient Advocate
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Nikki McIntoch, mother of a boy with spinal muscular atrophy (SMA) and founder of the advocacy group Rare Mamas.
16 Sep 202511min
189: An Interview With Dr. Jennifer Brown, Director of the CLL Center at Dana-Farber Cancer Institute
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jennifer Brown, MD, PhD, director of the CLL Center at Dana-Farber Cancer Institute in Boston, Massachusetts, and winner of the ...
8 Sep 202513min
188: An Interview With Michio Hirano, MD, a Global Expert on Thymidine Kinase 2 Deficiency
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews neurologist Michio Hirano, MD, of Columbia University in New York about an investigative therapy that shows promise in treating ...
3 Sep 20258min
187: An Interview With Dr. Pradeep P.A. Mammen on Females With Duchenne Muscular Dystrophy
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews cardiologist Pradeep P.A. Mammen, MD, of the University of Kansas School of Medicine, on the growing awareness of girls affected...
27 Aug 202512min
186: An Interview With Kfir Oved, CEO of Canopy Biotech, Which is Pursuing Novel Treatments in MG
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Kfir Oved about the latest Israeli research on myasthenia gravis.
18 Aug 202515min
