
Advocating for People With Gastrointestinal Stromal Tumor
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Knox, senior research director at the Life Raft Group. Based in Wayne, New Jersey, this organization was incorporated in 2...
31 Aug 202130min

2: Dr. Mark Brantly on Treating AATD and the Work of the Alpha-1 Foundation
17 Aug 202111min

1: Ultragenyx CMO Dr. Camille Bedrosian Discusses the First FDA-Approved Treatment for LCFAOD
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Camille Bedrosian, MD, chief medical officer and executive vice president of Ultragenyx Pharmaceutical in Novato, California. Ea...
11 Aug 202114min


















