Perspectives on Long Chain Fatty Oxidation Disorder With Dr. Jerry Vockley
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jerry Vockley, MD, PhD, chief of medical genetics at Pennsylvania's UPMC Children's Hospital of Pittsburgh. Dr. Vockley is also ...
23 Sep 202125min
6: Dr. Hagit Baris-Feldman Discusses Israel's Burgeoning Role in Rare Disease Clinical Research
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Hagit Baris-Feldman, MD, director of the Genetics Institute at Israel's Tel Aviv Sourasky Medical Center. Dr. Baris-Feldman, who...
22 Sep 202113min
5: Dr. Noah Greenspan Discusses on the Diagnosis and Treatment of Patients With PAH
17 Sep 202116min
Dr. Barry Byrne on Recent Developments in Pompe Disease
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Barry Byrne, MD, director of the University of Florida's Powell Gene Therapy Center in Gainesville. Dr. Byrne has spent years re...
13 Sep 202114min
4: Dr. Eric Olson Discusses the Use of Gene Therapy in the Treatment of Duchenne Muscular Dystrophy
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Eric Olson, PhD, chief scientific advisor at Vertex Pharmaceuticals and founding chair of the molecular biology department at th...
8 Sep 20219min
3: An Interview With Dr. Edward Neilan, Chief Medical Officer at NORD
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Edward Neilan, MD, chief medical officer at the National Organization for Rare Disorders (NORD). This is a new position at NORD,...
7 Sep 202121min
An Update on LAL-D With Dr. Paul Martin of Nationwide Children's Hospital
1 Sep 202114min
Insights From Dr. Noah Greenspan: Diagnosing and Treating IPF
1 Sep 202122min
