SMA News & Perspectives

SMA News & Perspectives

Daily, digital coverage of the latest SMA news and perspectives.

Den här podcasten är hämtad från ett öppet RSS-flöde och publiceras inte av Podme. Den kan innehålla reklam.

Avsnitt(446)

Newborn Screening in Massachusetts Seen as Highly Accurate And Effective

Newborn Screening in Massachusetts Seen as Highly Accurate And Effective

SMA News Today’s multimedia associate, Price Wooldridge, discusses newborn screening for Spinal Muscular Atrophy (SMA) in Massachusetts being seen as highly accurate and effective. Forums Director Ke...

30 Juni 202110min

Spinraza Leads to Better Swallowing, Farther Walking & Weekly Wins: Sharing Wins in Our Forums

Spinraza Leads to Better Swallowing, Farther Walking & Weekly Wins: Sharing Wins in Our Forums

SMA News Today’s multimedia associate, Price Wooldridge, discusses children with Spinal Muscular Atrophy (SMA) taking Spinraza, leanding to better swallowing and farther walking. Also, not only are t...

28 Juni 20217min

Apitegromab Safely Increases Motor Abilities in SMA Types 2, 3

Apitegromab Safely Increases Motor Abilities in SMA Types 2, 3

SMA News Today’s multimedia associate, Price Wooldridge, discusses meaningful improvements in motor abilities evident with apitegromab treatment in later-onset Spinal Muscular Atrophy (SMA) patients. ...

25 Juni 20218min

Evrysdi Linked to Improved Motor Function in 2 Trials & Finding Community Support

Evrysdi Linked to Improved Motor Function in 2 Trials & Finding Community Support

SMA News Today’s multimedia associate, Price Wooldridge, discusses Evrysdi being linked to motor function improvements in a broad range of people with Spinal Muscular Atrophy (SMA). Also, Forums Dire...

23 Juni 202111min

SMA Added to North Carolina’s Newborn Screening Program

SMA Added to North Carolina’s Newborn Screening Program

SMA News Today’s multimedia associate, Price Wooldridge, discusses adding a Spinal Muscular Atrophy (SMA) newborn screening program in North Carolina. Also, DeAnn Runge shares, Halsey Blocher’s lates...

21 Juni 20218min

NICE Favors Zolgensma Being Added to England’s Public Health Program

NICE Favors Zolgensma Being Added to England’s Public Health Program

SMA News Today’s multimedia associate, Price Wooldridge, discusses NICE issuing its final Zolgensma appraisal for eligible Spinal Muscular Atrophy (SMA) patients. For the second time the Cure SMA con...

18 Juni 20217min

Navigating the Past Year Without Caregivers Has Been Challenging

Navigating the Past Year Without Caregivers Has Been Challenging

SMA News Today’s multimedia associate, Price Wooldridge, reads the column by Alyssa Silva, Life, One Cup At a Time, “Navigating the Past Year Without Caregivers Has Been Challenging”. Also, Forums D...

16 Juni 20218min

#84: Scholar Rock Updates and Embracing the Growing Pains of New Wheels

#84: Scholar Rock Updates and Embracing the Growing Pains of New Wheels

In episode 84, host Kevin Schaefer talks with fellow SMA News Today contributors Michael Morale and DeAnn Runge. They discuss some topics from the 2021 virtual Cure SMA conference and general news upd...

15 Juni 202147min

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