SMA News & Perspectives

SMA News & Perspectives

Daily, digital coverage of the latest SMA news and perspectives.

Den här podcasten är hämtad från ett öppet RSS-flöde och publiceras inte av Podme. Den kan innehålla reklam.

Avsnitt(445)

Grant Awarded to Find Affordable Treatments for Children & SMA Would You Rather

Grant Awarded to Find Affordable Treatments for Children & SMA Would You Rather

SMA News Today’s multimedia associate, Price Wooldridge, discusses a grant awared to find affordable treatments for children with Spinal Muscular Atrophy (SMA). Also, on the forums a fun game of SMA ...

10 Maj 20215min

Novartis Poised for Phase 3b SMART Study of Zolgensma & SMA Adventures

Novartis Poised for Phase 3b SMART Study of Zolgensma & SMA Adventures

SMA News Today’s multimedia associate, Price Wooldridge, discusses how Novartis is poised for their Phase 3b SMART study of Zolgensma. Also, DeAnn Runge shares a recent adventure she went on to a gre...

7 Maj 20219min

Danish Family Races to Raise $2.4M for Daughter’s Zolgensma Therapy & Staying True To Yourself

Danish Family Races to Raise $2.4M for Daughter’s Zolgensma Therapy & Staying True To Yourself

SMA News Today’s multimedia associate, Price Wooldridge, discusses a Danish family raising $2.4 million for their daughter’s Zolgensma therapy. Also, Kevin Schaefer reads a column about staying true ...

5 Maj 202112min

#81: Interview With Chaz Hayden - Writer and YouTuber with SMA

#81: Interview With Chaz Hayden - Writer and YouTuber with SMA

In episode 81, host Kevin Schaefer talks with Chaz Hayden from Princeton, New Jersey. Chaz is a writer and YouTuber with SMA. He talks about growing up with SMA, starting college at a young age, and h...

4 Maj 202138min

#AANAM – Zolgensma May Lead to Faster, Greater Gains Than Spinraza

#AANAM – Zolgensma May Lead to Faster, Greater Gains Than Spinraza

SMA News Today’s multimedia associate, Price Wooldridge, discusses how Zolgensma may lead to faster, greater gains than Spinraza in Spinal Muscular Atrophy (SMA) infants. Also, DeAnn Runge reads an a...

3 Maj 202111min

Neurofilaments Before Spinraza May Predict Motor Improvements & Reviewing The Sound of Metal

Neurofilaments Before Spinraza May Predict Motor Improvements & Reviewing The Sound of Metal

SMA News Today’s multimedia associate, Price Wooldridge, discusses neurofilaments, before beginning Spinraza, may predict motor improvements in children with Spinal Muscular Atrophy (SMA). Also, DeAn...

30 Apr 20219min

Health Canada Approves Evrysdi for At-home Treatment

Health Canada Approves Evrysdi for At-home Treatment

SMA News Today’s multimedia associate, Price Wooldridge, discusses Health Canada’s approval of Evrysdi for at-home treatment in SMA patients. Also, Forums Director Kevin Schaefer reads a column by Ar...

28 Apr 20218min

Immune Response to Zolgensma Can Be Common in Older SMA Children

Immune Response to Zolgensma Can Be Common in Older SMA Children

SMA News Today’s multimedia associate, Price Wooldridge, discusses the immune reponse to Zolgensma can be common in older Spinal Muscular Atrophy (SMA) children. Also, SMA News Today content creator ...

26 Apr 20219min

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