Acute Liver Failure Warning Added to Zolgensma Label & Time Management and SMA
SMA News Today’s multimedia associate, Price Wooldridge, discusses how the U.S. FDA has added acute liver failure to the list of concerns with use of Zolgensma in children with spinal muscular atrophy...
9 Joulu 20219min
Oral SMA Therapy Is Ideal and Aids Motor Skills and Breathing & Why No Changes in SMA is Good
SMA News Today’s multimedia associate, Price Wooldridge, discusses how better/stable motor function and breathing, along with oral use, is ranked high in a UK survey of SMA type 2 and 3 adult patients...
6 Joulu 202111min
#93: Interview With Garrett Lerner, Co-creator and Executive Producer of NBC Series “Ordinary Joe”
In episode 93, host Kevin Schaefer talks with Garrett Lerner from Los Angeles, California. Garrett is the co-creator and co-showrunner of the NBC drama series “Ordinary Joe,” and he is a father to a s...
2 Marras 202144min
Phase 3 Apitegromab Trial Planned for Non-ambulatory Types 2 And 3 & Latest Topics on Our Forums
SMA News Today’s multimedia associate, Price Wooldridge, discusses an article on how Scholar Rock plans to initiate a Phase 3 trial of apitegromab in spinal muscular atrophy types 2 and 3 patients una...
28 Loka 20217min
Neurofilament Blood Levels Likely to Predict Treatment Response in SMA
SMA News Today’s multimedia associate, Price Wooldridge, discusses a news article on how blood levels of phosphorylated neurofilament heavy chain, nerve cell damage marker, are related to greater moto...
25 Loka 20219min
Quality of Life Survey Aims to Help Inform SMA Community Needs & Situations That Could’ve Gone Wrong
SMA News Today’s multimedia associate, Price Wooldridge, reads the SMA News Today article, “New Quality of Life Survey Aims to Help Inform SMA Community Needs”. Also, over on the forums there was jus...
21 Loka 20218min
#92: Discussing Disability and Employment
In episode 92, host Kevin Schaefer talks with fellow SMA News Today contributors to discuss each other’s work experiences. October is recognized in the United States as National Disability Employment ...
19 Loka 202147min
Pre-symptomatic Infants Retain Swallowing Ability in Evrysdi Trial
SMA News Today’s multimedia associate, Price Wooldridge, reads an article on how pre-symptomatic infants with SMA have retained the ability to swallow after being treated with Evrysdi for at least one...
18 Loka 20216min
