SMA Candidate SRK-015 Shows Promise in Healthy Volunteers & More Independence
SMA News Today’s Director of Multichannel Content, Michael Morale, discusses an ongoing trial that states how SMA candidate SRK-015 shows promise in healthy volunteers and Community Development Manage...
11 Syys 201910min
Study Says Children With SMA Are at Risk of Weak Bones And Fractures & More Independence
We discuss a study that suggests children with SMA are at risk of weak bones and fractures and Community Development Manager Kevin Schaefer talks about his journey toward more independence. Are you i...
9 Syys 20199min
How AveXis’ OneGene Program Could Help Families Wanting Zolgensma & Trending Topics
We discuss how AveXis’ OneGene program could smooth the path for families wanting Zolgensma and Community Development Manager Kevin Schaefer talks about some trending discussions in the SMA News Today...
6 Syys 20199min
Future Work Into Zolgensma, Gene Therapy And Other SMA Treatments & Physical Books
SMA News Today’s Director of Multichannel Content, Michael Morale, discusses likely future work into Zolgensma, gene therapies and other SMA treatments. Community Development Manager Kevin Schaefer ta...
4 Syys 201912min
#41 - Roundtable Discussion - Discussion for September 2019
Hosts Kevin Schaefer and Michael Morale discuss a recent webinar about AveXis’ gene therapy Zolgensma. Then in part two, they talk about SMA awareness month, and a couple of our recent columns.
3 Syys 201931min
NORD Honors Industry In Patient Advocates At Rare Impact Awards Gala & Overprotective Parents
We discuss how NORD honors industry in patient advocates at rare impact awards gala and SMA News Today forums moderator DeAnn Runge shares her perspective on overprotective parents. A college friend i...
2 Syys 20198min
Anti-Epileptic Keppra Can Be A Candidate For SMA Treatment & Batcave For Personal Space
We discuss a study that suggests that suggests Anti-epileptic Keppra could be a candidate for treatment of SMA and Community Development Manager Kevin Schaefer reads his latest column about acquiring ...
30 Elo 20198min
Zolgensma’s Arrival Adds Urgency to SMA Newborn Screening Efforts & Natalie Russo And Her Brother
SMA News Today’s Director of Multichannel Content, Michael Morale, discusses how Zolgensma’s arrival adds urgency to SMA newborn screening efforts in the US and Community Development Manager Kevin Sch...
28 Elo 20199min
